Liver-specific nucleic acid regulatory elements and methods and use thereof
作者： Pieter De Bleser , Marinee Chuah , Thierry Vandendriessche
DOI:
关键词: Nucleic acid 、 Biochemistry 、 Gene 、 Biology 、 Genetic enhancement
摘要: The present invention relates to nucleic acid regulatory elements that are able enhance liver-specific expression of genes, methods employing these and uses elements. Expression cassettes vectors containing also disclosed. is particularly useful for applications using gene therapy.
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