Opportunities for the use of lentiviral vectors in human gene therapy.
作者： F. Galimi , I. M. Verma
DOI: 10.1007/978-3-642-56114-6_13
关键词: Metachromatic leukodystrophy 、 Computational biology 、 Retinitis pigmentosa 、 Vector (molecular biology) 、 Genetic enhancement 、 Ciency virus 、 Gene delivery 、 Delivery system 、 Medicine
摘要: The quest for the perfect delivery system has been one of leitmotivs in young history gene therapy. Remarkable progress vector design generated a number distinct viral and nonviral tools, each manifesting advantages limitations.
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