Nanovesicle-Mediated Delivery Systems for CRISPR/Cas Genome Editing.
作者： Dongyoon Kim , Quoc-Viet Le , Yina Wu , Jinwon Park , Yu-Kyoung Oh
DOI: 10.3390/PHARMACEUTICS12121233
关键词: Extracellular vesicles 、 Subgenomic mRNA 、 Biology 、 Computational biology 、 CRISPR 、 Therapeutic modalities 、 Incurable diseases 、 Genome editing
摘要: … sgRNA through endosome escape or using … exosome, GFP-fused exosomes were found to carry a significantly higher amount of sgRNA/Cas9 complex compared with plain exosomes. …
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Anne-Kathrin Dreyer, Dirk Hoffmann, Nico Lachmann, Mania Ackermann, Doris Steinemann, Barbara Timm, Ulrich Siler, Janine Reichenbach, Manuel Grez, Thomas Moritz, Axel Schambach, Toni Cathomen, TALEN-mediated functional correction of X-linked chronic granulomatous disease in patient-derived induced pluripotent stem cells Biomaterials. ,vol. 69, pp. 191- 200 ,(2015) , 10.1016/J.BIOMATERIALS.2015.07.057
Jung Soo Suk, Qingguo Xu, Namho Kim, Justin Hanes, Laura M. Ensign, PEGylation as a strategy for improving nanoparticle-based drug and gene delivery Advanced Drug Delivery Reviews. ,vol. 99, pp. 28- 51 ,(2016) , 10.1016/J.ADDR.2015.09.012
Luigi Naldini, Gene therapy returns to centre stage Nature. ,vol. 526, pp. 351- 360 ,(2015) , 10.1038/NATURE15818
Ru Cheng, Fang Feng, Fenghua Meng, Chao Deng, Jan Feijen, Zhiyuan Zhong, Glutathione-responsive nano-vehicles as a promising platform for targeted intracellular drug and gene delivery. Journal of Controlled Release. ,vol. 152, pp. 2- 12 ,(2011) , 10.1016/J.JCONREL.2011.01.030
Masamitsu Kanada, Michael H. Bachmann, Jonathan W. Hardy, Daniel Omar Frimannson, Laura Bronsart, Andrew Wang, Matthew D. Sylvester, Tobi L. Schmidt, Roger L. Kaspar, Manish J. Butte, A. C. Matin, Christopher H. Contag, Differential fates of biomolecules delivered to target cells via extracellular vesicles Proceedings of the National Academy of Sciences of the United States of America. ,vol. 112, pp. 201418401- ,(2015) , 10.1073/PNAS.1418401112
Sung Mook Lim, Dae Kun Song, Se Heang Oh, Dong Sin Lee-Yoon, Eun Hee Bae, Jin Ho Lee, In vitro and in vivo degradation behavior of acetylated chitosan porous beads. Journal of Biomaterials Science-polymer Edition. ,vol. 19, pp. 453- 466 ,(2008) , 10.1163/156856208783719482
F Ann Ran, Patrick D Hsu, Jason Wright, Vineeta Agarwala, David A Scott, Feng Zhang, Genome engineering using the CRISPR-Cas9 system Nature Protocols. ,vol. 8, pp. 2281- 2308 ,(2013) , 10.1038/NPROT.2013.143
Zhijian Wu, Hongyan Yang, Peter Colosi, Effect of Genome Size on AAV Vector Packaging Molecular Therapy. ,vol. 18, pp. 80- 86 ,(2010) , 10.1038/MT.2009.255
Sang Myoung Noh, Su Eun Han, Gayong Shim, Kyoung Eun Lee, Chan-Wha Kim, Sung Sik Han, Yongseok Choi, Young Keun Kim, Won-Ki Kim, Yu-Kyoung Oh, Tocopheryl oligochitosan-based self assembling oligomersomes for siRNA delivery Biomaterials. ,vol. 32, pp. 849- 857 ,(2011) , 10.1016/J.BIOMATERIALS.2010.09.027
Fyodor D. Urnov, Edward J. Rebar, Michael C. Holmes, H. Steve Zhang, Philip D. Gregory, Genome editing with engineered zinc finger nucleases Nature Reviews Genetics. ,vol. 11, pp. 636- 646 ,(2010) , 10.1038/NRG2842