Hematopoietic Stem Cell Transplantation Beyond Severe Combined Immunodeficiency: Seeking a Cure for Primary Immunodeficiency
作者： Richard Mitchell
DOI: 10.1016/J.JAIP.2018.12.011
关键词:
摘要: Hematopoietic stem cell transplantation (HSCT) can provide definitive therapy for patients with primary immunodeficiency disease (PIDD). Modern HSCT techniques and supportive care have significantly improved outcomes PIDD. This review examines current practice PIDD other than severe combined immunodeficiency, explores indications, risks, long-term this group of challenging diseases.
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