Gene Therapy of Lysosomal Storage Disorders by Lentiviral Vectors

Antonia Follenzi, Luigi Naldini, HIV-based vectors. Preparation and use. Methods in molecular medicine. ,vol. 69, pp. 259- 274 ,(2002) , 10.1385/1-59259-141-8:259

David W. Kennedy, Janis L. Abkowitz, Kinetics of Central Nervous System Microglial and Macrophage Engraftment: Analysis Using a Transgenic Bone Marrow Transplantation Model Blood. ,vol. 90, pp. 986- 993 ,(1997) , 10.1182/BLOOD.V90.3.986

Thomas M. Daly, AAV-Mediated Gene Transfer to the Liver Methods of Molecular Biology. ,vol. 246, pp. 195- 199 ,(2004) , 10.1385/1-59259-650-9:195

J. A. Barranger, E. O'Rourke, Lessons learned from the development of enzyme therapy for Gaucher disease. Journal of Inherited Metabolic Disease. ,vol. 24, pp. 89- 96 ,(2001) , 10.1023/A:1012440428282

Antonia Follenzi, Luigi Naldini, Generation of HIV-1 derived lentiviral vectors. Methods in Enzymology. ,vol. 346, pp. 454- 465 ,(2002) , 10.1016/S0076-6879(02)46071-5

A. Espinosa de los Monteros, H. Baba, P. M. Zhao, T. Pan, R. Chang, J. de Vellis, K. Ikenaka, Remyelination of the adult demyelinated mouse brain by grafted oligodendrocyte progenitors and the effect of B-104 cografts. Neurochemical Research. ,vol. 26, pp. 673- 682 ,(2001) , 10.1023/A:1010943505013

Mark A. Kay, Joseph C Glorioso, Luigi Naldini, Viral vectors for gene therapy: the art of turning infectious agents into vehicles of therapeutics Nature Medicine. ,vol. 7, pp. 33- 40 ,(2001) , 10.1038/83324

R Charles Scriver, The Metabolic and Molecular Bases of Inherited Disease ,(1995)

Guillermo Guenechea, Olga I. Gan, Craig Dorrell, John E. Dick, Distinct classes of human stem cells that differ in proliferative and self-renewal potential. Nature Immunology. ,vol. 2, pp. 75- 82 ,(2001) , 10.1038/83199

Josef Priller, Alexander Flügel, Tim Wehner, Matthias Boentert, Carola A. Haas, Marco Prinz, Francisco Fernández-Klett, Konstantin Prass, Ingo Bechmann, Bauke A. de Boer, Michael Frotscher, Georg W. Kreutzberg, Derek A. Persons, Ulrich Dirnagl, Targeting gene-modified hematopoietic cells to the central nervous system: Use of green fluorescent protein uncovers microglial engraftment Nature Medicine. ,vol. 7, pp. 1356- 1361 ,(2001) , 10.1038/NM1201-1356