Compositions and methods for making therapies delivered by viral vectors reversible for safety and allele-specificity
作者： William F. Kaemmerer , Jennifer Heisel , Deepak Thakker , Eric Burright
DOI:
关键词:
摘要: The present invention is directed to compositions, methods and kits for regulation of gene therapies Huntington's Disease, including, without limitation, reversible allele-specific therapies.
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