Methods for treating lysosomal acid lipase deficiency
作者： Michael Concino , Michael Heartlein , Pericles Calias , Brian Felice , Nancy Savioli
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摘要: The present invention provides compositions and methods for effective treatment of a lysosomal acid lipase deficiency (LALD) disease, in particular, Wolman's disease Cholesteryl Ester Storage Disease (CESD). Among other things, the method treating developmental impairment or malnutrition an individual suffering from comprising administering to therapeutic amount lipase.
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