Three-Year Follow-up after Unilateral Subretinal Delivery of Adeno-Associated Virus in Patients with Leber Congenital Amaurosis Type 2
作者： Francesco Testa , Albert M. Maguire , Settimio Rossi , Eric A. Pierce , Paolo Melillo
DOI: 10.1016/J.OPHTHA.2012.11.048
关键词:
摘要: … delivery of adeno-associated virus (AAV2-hRPE65v2). Subjects were evaluated before and … improvements after a single unilateral subretinal injection of the AAV2-hRPE65v2 vector. …
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