Amit C. Nathwani, Ulreke M. Reiss, Edward G.D. Tuddenham, Cecilia Rosales, Pratima Chowdary, Jenny McIntosh, Marco Della Peruta, Elsa Lheriteau, Nishal Patel, Deepak Raj, Anne Riddell, Jun Pie, Savita Rangarajan, David Bevan, Michael Recht, Yu-Min Shen, Kathleen G. Halka, Etiena Basner-Tschakarjan, Federico Mingozzi, Katherine A. High, James Allay, Mark A. Kay, Catherine Y.C. Ng, Junfang Zhou, Maria Cancio, Christopher L. Morton, John T. Gray, Deokumar Srivastava, Arthur W. Nienhuis, Andrew M. Davidoff,
Long-term safety and efficacy of factor IX gene therapy in hemophilia B The New England Journal of Medicine. ,vol. 371, pp. 1994- 2004 ,(2014) ,
10.1056/NEJMOA1407309