Valproic acid increases the SMN2 protein level: a well-known drug as a potential therapy for spinal muscular atrophy
作者： L Brichta , Y Hofmann , E Hahnen , FA Siebzehnrubl , H Raschke
DOI: 10.1093/HMG/DDG256
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摘要: … Importantly, this up-regulation of SMN could be most likely attributed to increased levels of Htra2-β1 which facilitates the correct splicing of SMN2 RNA as well as to an SMN gene …
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