A majority of Huntington's disease patients may be treatable by individualized allele-specific RNA interference
作者： Maria Stella Lombardi , Leonie Jaspers , Christine Spronkmans , Cinzia Gellera , Franco Taroni
DOI: 10.1016/J.EXPNEUROL.2009.03.004
关键词:
摘要: … SNPs for which allele-specific siRNA should be sought, and demonstrate that allele-specific siRNAs can be found for a number of these SNP … rates for five of the six SNPs for which we …
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