Tuberous sclerosis treatment
作者： Ingrid Elmroth , Michael Stumm , Heidi Lane , William Berg , William Sellers
DOI:
关键词:
摘要: PROBLEM TO BE SOLVED: To provide a compound, etc. for the use of treating and preventing neurocutaneous disorders, like mediated via tuberous sclerosis complex, e.g., neurofibromatosis type 1.SOLUTION: There are provided rapamycin derivative formula I [wherein, Ris CHor 3-6C alkynyl; H, -CH-CH-OH or -CH-CH-O-(1-8C) alkyl, -CH-CH-O-CH-CH; X is =O, (H, H) OH), wherein when =O CH, not H] provided, pharmaceutical composition containing same.
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