Engineering liver-detargeted AAV9 vectors for cardiac and musculoskeletal gene transfer.
作者： Nagesh Pulicherla , Shen Shen , Swati Yadav , Kari Debbink , Lakshmanan Govindasamy
DOI: 10.1038/MT.2011.22
关键词:
摘要: … In the current study, we have identified novel liver-detargeted variants of AAV9 using comprehensive structural analysis and in vivo screening. Similar variants of other AAV serotypes …
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sci-hub.se 参考文章(46)
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