Unraveling the Complex Story of Immune Responses to AAV Vectors Trial After Trial

作者: Céline Vandamme , Oumeya Adjali , Federico Mingozzi

DOI: 10.1089/HUM.2017.150

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摘要: … responses The initial report of a deleterious effect of antiAAV cellular immune responses was the first clinical trial of liver-directed gene transfer for hemophilia B40 (Fig. 2). The FIX …

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