TYROSINE-MODIFIED RECOMBINANT rAAV VECTOR COMPOSITIONS AND METHODS FOR USE
作者： Mavis Agbandje-McKenna , Lakshmanan Govindasamy , Sergei Zolotukhin , Arun Srivastava , Li Zhong
DOI:
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摘要: Disclosed are tyrosine-modified rAAV vectors, as well infectious virions, compositions, and pharmaceutical formulations that comprise them. Also disclosed methods of preparing for using the tyrosine-phosphorylated capsid protein mutant vectors in a variety diagnostic therapeutic applications including vivo ex gene therapy, large-scale production vectors.
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