On the front of X-linked adrenoleukodystrophy.

作者: Patrick Aubourg

DOI: 10.1023/A:1022583813171

关键词:

摘要: The profound and lasting involvement of Hugo Ann Moser have allowed to make remarkable progress in adrenoleulodystrophy (ALD) during the last 20 years. Besides their own commitment ALD, constantly encouraged physicians, biologists molecular geneticists undertake clinical fundamental research this devastating disease. There is now some preventive therapeutic approaches which can be proposed ALD patients families. issues that still remain unresolved will certainly keep busy those who share «Hugo spirit».

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