ANTISENSE OLIGONUCLEOTIDE CAPABLE OF CANCELLING INTRON RETENTION IN DYSTROPHIN GENE
作者： Matsuo Masafumi , Koizumi Makoto
DOI:
关键词: Dystrophin gene 、 Dystrophin 、 Molecular biology 、 Intron 、 Chemistry 、 Antisense oligonucleotides
摘要: Provided is a compound which can cancel the intron retention in dystrophin gene to promote expression of dystrophin. An antisense oligonucleotide capable cancelling gene, or pharmaceutically acceptable salt solvate thereof. A pharmaceutical composition containing therapeutic agent for disease occurs, comprises
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