Compositions and methods for treating transthyretin (ttr) mediated amyloidosis
作者： Jared Gollob
DOI:
关键词: Human patient 、 Medicine 、 Transthyretin 、 Amyloidosis 、 Pathology
摘要: Disclosed herein are methods for treating hereditary transthyretin-mediated amyloidosis (hATTR amyloidosis) in a human patient need thereof by administering an effective amount of transthyretin (TTR)-inhibiting composition.
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