The Evolving Druggability and Developability Space: Chemically Modified New Modalities and Emerging Small Molecules

作者: Wenzhan Yang , Prajakta Gadgil , Venkata R. Krishnamurthy , Margaret Landis , Pankajini Mallick

DOI: 10.1208/S12248-019-0402-2

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摘要: … In addition, the question mark, “?”, was used for properties where there is a potential risk and a … success of ASOs and siRNAs along with the therapeutic potential of mRNA and CRISPR-…

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