Compositions and methods for treating non-age-associated hearing impairment in a human subject
作者： Ellen Reisinger , Robert Ng , Emmanuel John Simons
DOI:
关键词: Medicine 、 Hearing loss 、 Subject (documents) 、 Computational biology 、 Coding region 、 Nucleic acid
摘要: Provided herein are compositions that include at least two different nucleic acid vectors, where each of the vectors includes a coding sequence encodes portion an otoferlin protein, and use these to treat hearing loss in subject.
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