Augmenting Vitamin D to Combat Genetic Disease

作者: Blake R. Peterson

DOI: 10.1016/S1074-5521(02)00287-9

关键词:

摘要: Vitamin D-resistant rickets is a genetic disease that causes severe bone underdevelopment due to mutations in the vitamin D receptor. Orthogonal analogs of were recently identified correct defects ligand binding pocket mutant receptor associated with this disease.

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