Antisense Oligonucleotide-Based Therapies for Diseases Caused by pre-mRNA Processing Defects
作者： Frank Rigo , Punit P. Seth , C. Frank Bennett
DOI: 10.1007/978-1-4939-1221-6_9
关键词:
摘要: Before a messenger RNA (mRNA) is translated into a protein in the cytoplasm, its pre-mRNA precursor is extensively processed through capping, splicing and polyadenylation in the …
springer.com
sci-hub.st 参考文章(370)
Annemieke Aartsma-Rus, Overview on AON Design Methods of Molecular Biology. ,vol. 867, pp. 117- 129 ,(2012) , 10.1007/978-1-61779-767-5_8
David P Bartel, MicroRNAs: Genomics, Biogenesis, Mechanism, and Function Cell. ,vol. 116, pp. 281- 297 ,(2004) , 10.1016/S0092-8674(04)00045-5
Gabriela Ivanova, Sandrine Reigadas, Damian Ittig, Andrey Arzumanov, Marie-Line Andreola, Christian Leumann, Jean-Jacques Toulmé, Michael J. Gait, Tricyclo-DNA Containing Oligonucleotides as Steric Block Inhibitors of HIV-1 Tat-Dependent Trans Activation and HIV-1 Infectivity Mary Ann Liebert. ,(2007) , 10.1089/OLI.2006.0046
Robert P. Erickson, Jonathan G. Izant, Gene regulation : biology of antisense RNA and DNA Raven Press. ,(1992)
Jean Brachet, La détection histochimique et le microdosage des acides pentosenucléiques (tissus animaux - développement embryonnaire des amphibiens) Enzymologia. ,vol. 10, pp. 87- 96 ,(1941)
Maria Bitner-Glindzicz, Keith J Lindley, Paul Rutland, Diana Blaydon, Virpi V Smith, Peter J Milla, Khalid Hussain, Judith Furth-Lavi, Karen E Cosgrove, Ruth M Shepherd, Philippa D Barnes, Rachel E O'Brien, Peter A Farndon, Jane Sowden, Xue-Zhong Liu, Matthew J Scanlan, Sue Malcolm, Mark J Dunne, Albert Aynsley-Green, Benjamin Glaser, None, A recessive contiguous gene deletion causing infantile hyperinsulinism, enteropathy and deafness identifies the Usher type 1C gene Nature Genetics. ,vol. 26, pp. 56- 60 ,(2000) , 10.1038/79178
Sebastien A. Burel, So-Ri Han, Hong-Soo Lee, Daniel A. Norris, Byoung-Seok Lee, Todd Machemer, Shin-Young Park, Tianyuan Zhou, Guobin He, Youngsoo Kim, A. Robert MacLeod, Brett P. Monia, Shirley Lio, Tae-Won Kim, Scott P. Henry, Preclinical Evaluation of the Toxicological Effects of a Novel Constrained Ethyl Modified Antisense Compound Targeting Signal Transducer and Activator of Transcription 3 in Mice and Cynomolgus Monkeys Nucleic Acid Therapeutics. ,vol. 23, pp. 213- 227 ,(2013) , 10.1089/NAT.2013.0422
Aaron J. Shatkin, James L. Manley, The ends of the affair: capping and polyadenylation. Nature Structural & Molecular Biology. ,vol. 7, pp. 838- 842 ,(2000) , 10.1038/79583
B.P. Monia, J.F. Johnston, D.J. Ecker, M.A. Zounes, W.F. Lima, S.M. Freier, Selective inhibition of mutant Ha-ras mRNA expression by antisense oligonucleotides. Journal of Biological Chemistry. ,vol. 267, pp. 19954- 19962 ,(1992) , 10.1016/S0021-9258(19)88650-7
Hsiu Mei Hsieh-Li, Jan-Gowth Chang, Yuh-Jyh Jong, Mei-Hsiang Wu, Nancy M. Wang, Chang Hai Tsai, Hung Li, A mouse model for spinal muscular atrophy Nature Genetics. ,vol. 24, pp. 66- 70 ,(2000) , 10.1038/71709