Rare disease partnership: the role of the US HAEA in angioedema care.
作者： Bruce L. Zuraw , Sandra C. Christiansen
DOI: 10.1016/J.IAC.2013.07.011
关键词:
摘要: Rare diseases, including hereditary angioedema, present a unique set of challenges for clinicians and investigators. The most successful way to negotiate these difficulties has been develop collaborative efforts among physicians with patient advocacy organizations pharmaceutical companies. US Hereditary Angioedema Association is large nonprofit organization that the catalyst types arrangements involving angioedema. dedication structure this allowed it make substantial contribution improving angioedema diagnosis care.
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