Adenoviral vectors encoding erythropoietin and their use in gene therapy

作者: Rocco Savino , Gennaro Ciliberto , Nicola La Monica

DOI:

关键词: MedicineErythropoietinChronic renal failureImmunologyCellGenetic enhancement

摘要: Helper dependant adenoviral vectors encoding erythropoietin (epo) provide high levels of epo to achieve a long-term therapeutically effective dosage, and allow for repeat administration patients with disorders such as anaemia Chronic Renal Failure (CRF), anaemias due beta-thalassaemia, sickle cell (SCA).

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