David Adams, Alejandra Gonzalez-Duarte, William D. O’Riordan, Chih-Chao Yang, Mitsuharu Ueda, Arnt V. Kristen, Ivailo Tournev, Hartmut H. Schmidt, Teresa Coelho, John L. Berk, Kon-Ping Lin, Giuseppe Vita, Shahram Attarian, Violaine Planté-Bordeneuve, Michelle M. Mezei, Josep M. Campistol, Juan Buades, Thomas H. Brannagan, Byoung J. Kim, Jeeyoung Oh, Yesim Parman, Yoshiki Sekijima, Philip N. Hawkins, Scott D. Solomon, Michael Polydefkis, Peter J. Dyck, Pritesh J. Gandhi, Sunita Goyal, Jihong Chen, Andrew L. Strahs, Saraswathy V. Nochur, Marianne T. Sweetser, Pushkal P. Garg, Akshay K. Vaishnaw, Jared A. Gollob, Ole B. Suhr,
Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis The New England Journal of Medicine. ,vol. 379, pp. 11- 21 ,(2018) ,
10.1056/NEJMOA1716153